r/shares – CRSP ostensibly cures affected person of sickle cell anemia, the primary gene enhancing remedy to remedy a Mendelian dysfunction

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In a outstanding outcomes, CRSP exhibits that their gene enhancing remedy, utilizing the CRISPR-Cas9 expertise that just lately received its co-founder Emmanuelle Charpentier the 2020 Nobel Prize in chemistry, successfully cured one affected person of sickle cell anemia and one other of B-thalassemia. CRSP proclaims these leads to a chat on the American Society of Hematologists and in a publication within the premier medical journal- NEJM

https://www.nejm.org/doi/full/10.1056/NEJMoa2031054?query=featured_home

That is the primary time gene enhancing has cured a genetic illness in sufferers.

CRSP and the opposite gene enhancing shares EDIT, NTLA, and BEAM have had nice runs this 12 months, and their expertise has now been validated in a landmark examine.

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