The FDA has designated Orphan Drug standing to Ionis Prescription drugs’s (NASDAQ:IONS) ION373 for the therapy of Alexander illness, a uncommon neurodegenerative illness, characterised by the destruction of the myelin sheath (fatty protecting that protects the nerve fiber and helps sign conduction).
Alexander illness is brought on by a mutation in a protein leading to overproduction of glial fibrillary acidic protein (GFAP) within the mind, and ION373 is antisense medication designed to cease the mutated gene from producing extra GFAP.
